REVIEW 05-31-2012 - File 003
Actelion-InitiationBarclay 2010
Fabry Disease
New Treatment and Orphan Drug Development
Impact of Velaglucerase Alfa Therapy on Bone Marrow Burden Score in Adults with Type 1 Gaucher Disease: 7-Year Experience Deborah Elstein; 1 Andrew H.
ERT IN JUVENILE AND ADULT GLYCOGENOSIS TYPE 2 Bruno Bembi – Giovanni Ciana – Andrea Dardis Unità di Malattie Metaboliche-Laboratorio di Malattie Rare Istituto.
Document
Late Outcomes of Cord Blood Transplantation for Patients with Hurler Syndrome
Digestion & absorption of lipids
Fabry disease by Farshid Mokhberi
Global Gaucher Disease Market 2015-2019
Whole body MRI technique in early treated non-neuronopathic patients with enzyme replacement therapy at least eight years Larissa Moos, Jörg Reinke, Miriam.
